The U.S. Food and Drug Administration is tightening restrictions on a gene therapy used to treat Duchenne muscular dystrophy ...
Fred Hutch bioengineer Dr. Matthias Stephan is working to develop a special foam that could help make gene therapy for blood ...
The Food and Drug Administration is adding a new warning to a gene therapy linked to two patient deaths earlier this year.
Coave Therapeutics has announced its lead gene therapy program, CoTx-10, for the treatment of retinal vascular diseases, such ...
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Duchenne Gene Therapy: Why The FDA Has Tightened Rules Following Two Teen Deaths
The FDA has added a boxed warning to Sarepta’s Duchenne gene therapy Elevidys after two teens died from liver failure and has ...
Sarepta must also run a post-marketing study for Elevidys to better assess the risk of serious liver injury in patients dosed ...
MeiraGTx is cashing in on a gene therapy that restored vision to 11 children who were born legally blind, licensing the ...
A rare disease that has cut off children from the outside world now potentially has a cure. A clinical trial to treat severe ...
Penn and CHOP researchers want to develop urea cycle disorder treatments using CRISPR gene-editing therapy. Get unlimited access to Inquirer.com and The Inquirer App, plus 5 articles each month to ...
Two complementary studies led by researchers from the Yong Loo Lin School of Medicine, National University of Singapore (NUS ...
Taysha Gene Therapies Inc. (NASDAQ: TSHA) is a must-buy penny stock to buy now. On November 13, Piper Sandler analyst Biren ...
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