细胞与基因疗法 (Cell and Gene Therapy,CGT)正以前所未有的速度重塑现代医学的边界。自2017年首款 CART 疗法获批以来,CGT ...
The U.S. Food and Drug Administration is tightening restrictions on a gene therapy used to treat Duchenne muscular dystrophy ...
Fred Hutch bioengineer Dr. Matthias Stephan is working to develop a special foam that could help make gene therapy for blood ...
医学Medicine2025年10月23日,由复旦大学领衔的全球首个遗传性耳聋基因治疗国际专家共识在Cell Press细胞出版社旗下医学旗舰刊Med上正式发布[1],并登上Cell Press官网头条。论文题为“International ...
This story is part of a series on the current progression in Regenerative Medicine. In 1999, I defined regenerative medicine as the collection of interventions that restore tissues and organs damaged ...
Until recently, even the most advanced gene therapies could only be given after a child was born—often racing against time to prevent irreversible damage. In the first part of this series, we explored ...
By adding a microRNA molecule to ALS models, Tel Aviv University, Ben-Gurion University and Weizmann Institute researchers ...
The US FDA has tightened the use of a Duchenne muscular dystrophy gene therapy after two teenage patients died from acute ...
Sarepta must also run a post-marketing study for Elevidys to better assess the risk of serious liver injury in patients dosed ...
The Food and Drug Administration is adding a new warning to a gene therapy linked to two patient deaths earlier this year ...