The U.S. Food and Drug Administration is tightening restrictions on a gene therapy used to treat Duchenne muscular dystrophy ...
Genetic manipulation – or gene editing – is a concept that describes altering the genetic material (DNA) of an organism.
Penn and CHOP researchers will utilize the new protocol to distribute customizable drugs that target specific genetic disorders.
In a highly anticipated article, FDA officials Vinay Prasad, M.D., and Martin Makary, M.D., outlined a novel regulatory ...
Fred Hutch bioengineer Dr. Matthias Stephan is working to develop a special foam that could help make gene therapy for blood ...
Sarepta must also run a post-marketing study for Elevidys to better assess the risk of serious liver injury in patients dosed ...
Zacks Investment Research on MSN
FDA Restricts Use of Sarepta's Gene Therapy, Adds Safety Warnings
Sarepta Therapeutics SRPT announced that the FDA has approved significant changes to the label of Elevidys, its one-shot gene ...
The US FDA has tightened the use of a Duchenne muscular dystrophy gene therapy after two teenage patients died from acute ...
Cincinnati Children's Hospital has dedicated a new state-of-the-art facility for applied gene and cell therapy in Sharonville ...
The Times of Israel on MSN
In world first, Israeli scientists use RNA-based gene therapy to stop ALS deterioration
By adding a microRNA molecule to ALS models, Tel Aviv University, Ben-Gurion University and Weizmann Institute researchers ...
MeiraGTx is cashing in on a gene therapy that restored vision to 11 children who were born legally blind, licensing the ...
Sharonville, Ohio, celebrates the opening of the new Cincinnati Children's Applied Gene and Cell Therapy Center.
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