Scientists at St. Jude Children's Research Hospital and Northwestern University identified a previously unknown treatment ...

From revolutionary CRISPR treatment to heavy drinking dangers, here's what you need to know about the latest health research.

The FDA previously placed two clinical studies on hold, including the Phase III trial in which the liver toxicity occurred. Intellia is working with experts to create a risk management program for nex ...

Scientists discover a new gene therapy technique that may reverse ALS by restoring vital RNA signals, providing hope for ...

An experimental gene-editing therapy developed by Crispr Therapeutics is showing promise for treating heart disease.

N EW ORLEANS – A single injection of a gene-edited protein was deemed productive and safe in patients with dyslipidemia that ...

Opus Genetics has completed a Type B Regenerative Medicine Advanced Therapy (RMAT) meeting with the US Food and Drug Administration (FDA) regarding OPGx-LCA5, its gene therapy candidate for Leber ...

A new West Coast biotech has emerged into the busy in vivo cell therapy space, this time with the backing of Nobel Prize-winning CRISPR pioneer Jennifer Doudna, Ph.D. Azalea Therapeutics has bloomed ...

The inaugural Genetic Agency Technology Conference (GATC) gathered a group of researchers and entrepreneurs to discuss the vision for AI-based genetic medicine.

The agency is establishing a network of care centers to expand access to regenerative medicine beyond regions served by major ...