Fred Hutch bioengineer Dr. Matthias Stephan is working to develop a special foam that could help make gene therapy for blood ...

The approach is “very exciting,” but one expert says a lot more research is needed, especially around safety, before clinical ...

Scientists at St. Jude Children's Research Hospital and Northwestern University identified a previously unknown treatment ...

The gene therapies for cancer treatment market size was valued at US$ 11.59 billion in 2025 and is projected to grow to 16.22 billion in 2026. Forecasts suggest it will reach approximately US$ 238.77 ...

Gene therapy is a revolutionary approach to treating genetic disorders by introducing functional genes into cells to replace or correct defective genes. It involves the use of genetic material, such ...

Gene therapy is a revolutionary field in modern medicine, offering transformative potential to treat and potentially cure a wide range of genetic and acquired diseases. By addressing the root cause of ...

A CRISPR-based gene therapy showed improvement in lipids in difficult-to-treat patients, but one study raised flags after a death last month in a trial of an unrelated gene therapy.

In a 15-patient, Phase 1, first-in-human trial, a one-time CRISPR-Cas9 gene-editing therapy safely reduced LDL cholesterol ...

While gene therapy for cystic fibrosis is still in the research phase, researchers aim to correct the defective gene responsible for the disease. Current research is promising. Cystic fibrosis (CF) is ...

Researchers report early but encouraging results on an experimental gene-editing treatment for high cholesterol.

Broken String Biosciences ("Broken String"), a leader in advancing gene editing safety, today announced the appointment of ...