Coave Therapeutics has announced its lead gene therapy program, CoTx-10, for the treatment of retinal vascular diseases, such ...
Health and Me on MSN
Duchenne Gene Therapy: Why The FDA Has Tightened Rules Following Two Teen Deaths
The FDA has added a boxed warning to Sarepta’s Duchenne gene therapy Elevidys after two teens died from liver failure and has ...
The U.S. Food and Drug Administration is tightening restrictions on a gene therapy used to treat Duchenne muscular dystrophy ...
Penn and CHOP researchers will utilize the new protocol to distribute customizable drugs that target specific genetic disorders.
Through substantial leadership turnover and workforce cuts, the FDA has continued to support the advanced therapy sector, ...
Earlier this year, researchers at Children's Hospital of Philadelphia and Penn created a first-of-its-kind drug customized to ...
In medicine these days, the word "gene" shows up in all sorts of different contexts and conjugations. There's genetics, of course, and there's genomics. Then there's meta-genomics -- and don't forget ...
A rare disease that has cut off children from the outside world now potentially has a cure. A clinical trial to treat severe ...
The Times of Israel on MSN
In world first, Israeli scientists use RNA-based gene therapy to stop ALS deterioration
By adding a microRNA molecule to ALS models, Tel Aviv University, Ben-Gurion University and Weizmann Institute researchers ...
The US FDA has tightened the use of a Duchenne muscular dystrophy gene therapy after two teenage patients died from acute ...
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