After a meeting with the FDA, Scholar Rock is planning a 2026 resubmission of its application seeking approval of apitegromab ...

Like one of her favorite poems describes, columnist Brianna Albers always feels like she's digging herself out of a new hole in her life.

Zolgensma outperformed Spinraza in achieving a more sustained clinical response for children with SMA type 1, a comparative ...

Combining the experimental and approved SMA therapies BIO101 and Spinraza in the lab was found to improve muscle function in ...

Family caregivers express immense devotion to others, but they should also remember self-care, writes columnist.

Spinraza (nusinersen) may help stabilize lung function in people with SMA types 2 and 3, delaying the need for breathing ...

For columnist Alyssa Silva, control has always been her safety net. But in reality, it doesn't protect her; it exhausts her.

Most children SMA type 1 can survive an episode of pARDS, a life-threatening respiratory failure, under standard protocols, ...

When columnist Connie Chandler tackles an art project, it becomes a creative collaboration thanks to her supportive team of ...

Try these practical tips for travel with SMA, with advice on packing, accessible accommodations, and health management.

Spinal muscular atrophy (SMA) is a rare genetic condition characterized by progressive muscle weakness and atrophy. It mainly affects motor function, but often also causes problems with speaking, ...

Kevin Schaefer (he/him) is a writer, podcaster, and lover of all things pop culture. Diagnosed with SMA type 2 at the age of 18 months in 1995, he shares a vast array of hilarious and eye-opening ...