医学Medicine2025年10月23日，由复旦大学领衔的全球首个遗传性耳聋基因治疗国际专家共识在Cell Press细胞出版社旗下医学旗舰刊Med上正式发布[1]，并登上Cell Press官网头条。论文题为“International ...

细胞与基因疗法 (Cell and Gene Therapy，CGT)正以前所未有的速度重塑现代医学的边界。自2017年首款 CART 疗法获批以来，CGT ...

Fred Hutch bioengineer Dr. Matthias Stephan is working to develop a special foam that could help make gene therapy for blood ...

Coave Therapeutics has announced its lead gene therapy program, CoTx-10, for the treatment of retinal vascular diseases, such ...

This story is part of a series on the current progression in Regenerative Medicine. In 1999, I defined regenerative medicine as the collection of interventions that restore tissues and organs damaged ...

The FDA has added a boxed warning to Sarepta’s Duchenne gene therapy Elevidys after two teens died from liver failure and has ...

Until recently, even the most advanced gene therapies could only be given after a child was born—often racing against time to prevent irreversible damage. In the first part of this series, we explored ...

Sarepta must also run a post-marketing study for Elevidys to better assess the risk of serious liver injury in patients dosed ...

A rare disease that has cut off children from the outside world now potentially has a cure. A clinical trial to treat severe ...

The search for gene therapies to treat rheumatoid arthritis (RA) has moved in fits and starts over the past two decades, with trials starting and stopping, and their focus shifting to osteoarthritis ...