Risk of “acute, serious, and life-threatening” heart inflammation is now on the label of Sarepta's gene therapy for Duchenne ...

Corneal edema involves fluid accumulation in the cornea, leading to cloudiness and vision impairment. The market is growing due to an aging population and increasing cataract and glaucoma surgeries.

The global hemophilia market is experiencing robust growth, fueled by advances in gene therapy and recombinant clotting factors. Increased awareness and healthcare investment worldwide are expanding ...

A Greer couple is hosting a fundraiser to support a costly gene editing procedure for their two children, who suffer from a ...

They face a difficult choice, since the treatment may benefit their children but comes with serious risks and unknowns, particularly following reports of patient deaths.

Rocket Pharmaceuticals (RCKT) traded lower on Tuesday after J.P. Morgan downgraded the gene therapy developer to Underweight from Neutral, citing concerns over its mid-stage trial program for RP-A501, ...

Researchers have understood for decades that some forms of deafness are inherited, yet until now, few of those genetic clues ...