To manage the finances of CAR-T therapies, which can cost up to $1 million each, health systems are increasingly using “pay for performance” deals, according to a Nov. 17 article in Specialty Pharmacy ...

The gene therapy will utilize the firm's suprachoroidal vector coAAV-SCS, which it says will be an effective and less burdensome treatment alternative.

Thermo Fisher executives explain why they picked "Cellicon Valley" for the firm's second U.S. collaboration center and first ...

Researchers said a survey of U.S. adults found 72% say sleepiness sometimes, often or always gets in the way of their ...

Risk of “acute, serious, and life-threatening” heart inflammation is now on the label of Sarepta's gene therapy for Duchenne ...

Alzheimer's disease (AD) is a devastating cause of memory loss and cognitive decline, for which no curative treatment is ...

The FDA will mandate its strictest safety warning on Sarepta Therapeutics’ gene therapy for Duchenne muscular dystrophy, ...

A Greer couple is hosting a fundraiser to support a costly gene editing procedure for their two children, who suffer from a ...

They face a difficult choice, since the treatment may benefit their children but comes with serious risks and unknowns, particularly following reports of patient deaths.

Rocket Pharmaceuticals (RCKT) traded lower on Tuesday after J.P. Morgan downgraded the gene therapy developer to Underweight from Neutral, citing concerns over its mid-stage trial program for RP-A501, ...