This story is part of a series on the current progression in Regenerative Medicine. In 1999, I defined regenerative medicine as the collection of interventions that restore tissues and organs damaged ...
Labroots and the Cell & Gene Therapy planning committee are thrilled to announce the 2nd Annual Cell & Gene Therapy Virtual Event Series, live on October 15, 2025. This free, interactive event brings ...
Gene therapy is a revolutionary field in modern medicine, offering transformative potential to treat and potentially cure a wide range of genetic and acquired diseases. By addressing the root cause of ...
UCSF Benioff Children’s Hospital Oakland is enrolling patients in an innovative clinical trial that seeks to cure sickle cell disease. The trial is the first in the U.S. to apply non-viral CRISPR-Cas9 ...
A new gene therapy treatment for Duchenne muscular dystrophy (DMD) shows promise of not only arresting the decline of the muscles of those affected by this inherited genetic disease, but perhaps, in ...
While gene therapy for cystic fibrosis is still in the research phase, researchers aim to correct the defective gene responsible for the disease. Current research is promising. Cystic fibrosis (CF) is ...
MONDAY, Nov. 17, 2025 (HealthDay News) — The U.S. Food and Drug Administration (FDA) is tightening restrictions on a gene ...
Sarepta Therapeutics’ Elevidys will carry the FDA’s strongest warning label about the risks of liver damage and liver failure ...
The solution mitigates the financial impact of high-cost gene therapy claims. BOSTON--(BUSINESS WIRE)--One80 Intermediaries (One80), a specialty insurance broker headquartered in Boston, today ...