Earlier this year, researchers at Children's Hospital of Philadelphia and Penn created a first-of-its-kind drug customized to ...

Penn and CHOP researchers want to develop urea cycle disorder treatments using CRISPR gene-editing therapy. Get unlimited access to Inquirer.com and The Inquirer App, plus 5 articles each month to ...

In a highly anticipated article, FDA officials Vinay Prasad, M.D., and Martin Makary, M.D., outlined a novel regulatory ...

The FDA’s Marty Makary and Vinay Prasad have laid out a path for CRISPR treatments on demand. An expert weighs in on what it ...

Genetic manipulation – or gene editing – is a concept that describes altering the genetic material (DNA) of an organism.

WASHINGTON (AP) — Unapproved peptide drugs have become a trendy new hack among wellness influencers, fitness coaches and ...

The “plausible mechanism pathway” will allow personalised drugs to reach the market sooner for patients with genetic diseases ...

In this interview, Dr. Kelemen discusses the advantages of lipid-based delivery systems and their potential to expand the ...

The same pulling force that causes “tears” in a glass of wine also shapes embryos. It’s another example of how genes exploit ...

CTX310 showed promising safety and efficacy in a small Phase I trial, according to data presented at the American Heart ...

At Mayo Clinic, cardiologists Peter Noseworthy, M.D., and John Giudicessi, M.D., Ph.D., are uncovering the earliest signs of ...