Scientists discover a new gene therapy technique that may reverse ALS by restoring vital RNA signals, providing hope for ...

Scientists at St. Jude Children's Research Hospital and Northwestern University identified a previously unknown treatment ...

Scientists used a viral gene therapy to restore brain function in mice with SYNGAP1-related disorders, reducing seizures and behavioral symptoms.

Discover how precision biotherapeutics can transform healthcare in India by personalizing treatments based on genetic and ...

As Catalent sets up shop in a new headquarters and refines its corporate image under the ownership of Novo Holdings, the CDMO ...

NEW ORLEANS – A single injection of a gene-edited protein was deemed productive and safe in patients with dyslipidemia that ...

An experimental gene-editing therapy developed by Crispr Therapeutics is showing promise for treating heart disease.

Researchers at Tel Aviv University led a large-scale international study that opens a new avenue for treating the fatal ...

From revolutionary CRISPR treatment to heavy drinking dangers, here's what you need to know about the latest health research.

A report on gene-editing drugs renews debate around long-term statin use as Indian cardiologists caution that risk assessment ...

Opus Genetics has completed a Type B Regenerative Medicine Advanced Therapy (RMAT) meeting with the US Food and Drug Administration (FDA) regarding OPGx-LCA5, its gene therapy candidate for Leber ...

A new discovery from the lab of YouYang Zhao, Ph.D., from Stanley Manne Children's Research Institute at Ann & Robert H.