Fred Hutch bioengineer Dr. Matthias Stephan is working to develop a special foam that could help make gene therapy for blood ...

By adding a microRNA molecule to ALS models, Tel Aviv University, Ben-Gurion University and Weizmann Institute researchers ...

A single infusion of CRISPR Therapeutics' experimental gene therapy was safe and reduced levels of harmful LDL cholesterol ...

Earlier this year, researchers at Children's Hospital of Philadelphia and Penn created a first-of-its-kind drug customized to ...

Scientists at St. Jude Children's Research Hospital and Northwestern University identified a previously unknown treatment ...

Baby Muldoon, born with a rare genetic disorder, could not eliminate nitrogen compounds, causing toxic ammonia to accumulate ...

We have written about the promise of gene therapy to correct genetic disease many times. An exciting development happened ...

Emerging biotechnologies, strategic collaborations, and growing focus on personalized and regenerative medicine are accelerating the next wave of gene therapy innovation.Austin, Nov. 05, 2025 (GLOBE ...

In a first for adults in Singapore, scientists are conducting gene editing trials on heart patients to correct defects at their genetic source.

Despite the best efforts of modern medicine, Huntington’s disease is a condition that still comes with a tragic prognosis.

As a new €2 million gene therapy research project funded by APC and Research Ireland is announced, we speak with the project lead Prof Niall Barron about its potential and how Ireland is positioning ...