The world-class, low-cost gene editing solution named "BIRSA 101", in honour of Bhagwan Birsa Munda, remembered as a great ...

The U.S. Food and Drug Administration is tightening restrictions on a gene therapy used to treat Duchenne muscular dystrophy ...

Two complementary studies led by researchers from the Yong Loo Lin School of Medicine, National University of Singapore (NUS ...

先天性耳聋患者约2600万，常伴有言语障碍，甚至影响智力发育，一直以来没有临床治疗药物。2022年，复旦大学附属眼耳鼻喉科医院完成全球首例OTOF遗传性耳聋患者基因治疗，成为先天性耳聋首次基因治疗临床实践，成功恢复了患者听力。此后又有7项基因治疗临床 ...

In a world-first trial, scientists used a one-off CRISPR gene edit to switch off a liver “fat brake” gene, slashing stubborn ...

A Greer couple is hosting a fundraiser to support a costly gene editing procedure for their two children, who suffer from a ...

The Food and Drug Administration is adding a new warning to a gene therapy linked to two patient deaths earlier this year.

Despite the best efforts of modern medicine, Huntington’s disease is a condition that still comes with a tragic prognosis.

Researchers hope they are on track to find an innovative treatment effective against both a rare genetic disorder diagnosed ...

Researchers report early but encouraging results on an experimental gene-editing treatment for high cholesterol.

Fred Hutch bioengineer Dr. Matthias Stephan is working to develop a special foam that could help make gene therapy for blood ...

CRISPR gene-editing technology lets scientists make precise changes to an organism’s DNA. Invented in 2012 by Jennifer Doudna and Emmanuelle Charpentier, biochemists who went on to win the Nobel prize ...