The world-class, low-cost gene editing solution named "BIRSA 101", in honour of Bhagwan Birsa Munda, remembered as a great ...

The U.S. Food and Drug Administration is tightening restrictions on a gene therapy used to treat Duchenne muscular dystrophy ...

Two complementary studies led by researchers from the Yong Loo Lin School of Medicine, National University of Singapore (NUS ...

先天性耳聋患者约2600万，常伴有言语障碍，甚至影响智力发育，一直以来没有临床治疗药物。2022年，复旦大学附属眼耳鼻喉科医院完成全球首例OTOF遗传性耳聋患者基因治疗，成为先天性耳聋首次基因治疗临床实践，成功恢复了患者听力。此后又有7项基因治疗临床 ...

In a world-first trial, scientists used a one-off CRISPR gene edit to switch off a liver “fat brake” gene, slashing stubborn ...

A Greer couple is hosting a fundraiser to support a costly gene editing procedure for their two children, who suffer from a ...

A new biopharmaceutical company aims to identify better ways to make and analyse gene therapies, with potentially ...

Researchers hope they are on track to find an innovative treatment effective against both a rare genetic disorder diagnosed ...

The Food and Drug Administration is adding a new warning to a gene therapy linked to two patient deaths earlier this year.

Researchers report early but encouraging results on an experimental gene-editing treatment for high cholesterol.

CRISPR gene-editing technology lets scientists make precise changes to an organism’s DNA. Invented in 2012 by Jennifer Doudna and Emmanuelle Charpentier, biochemists who went on to win the Nobel prize ...

Fred Hutch bioengineer Dr. Matthias Stephan is working to develop a special foam that could help make gene therapy for blood ...