Earlier this year, researchers at Children's Hospital of Philadelphia and Penn created a first-of-its-kind drug customized to ...

The U.S. Food and Drug Administration is tightening restrictions on a gene therapy used to treat Duchenne muscular dystrophy ...

In medicine these days, the word "gene" shows up in all sorts of different contexts and conjugations. There's genetics, of course, and there's genomics. Then there's meta-genomics -- and don't forget ...

Penn and CHOP researchers will utilize the new protocol to distribute customizable drugs that target specific genetic disorders.

The Food and Drug Administration is adding a new warning to a gene therapy linked to two patient deaths earlier this year.

The US FDA has tightened the use of a Duchenne muscular dystrophy gene therapy after two teenage patients died from acute ...

Risk of “acute, serious, and life-threatening” heart inflammation is now on the label of Sarepta's gene therapy for Duchenne ...

Through substantial leadership turnover and workforce cuts, the FDA has continued to support the advanced therapy sector, ...

Krystal Biotech drives Vyjuvek growth, premium margins, global expansion, a $1B goal, and pipeline data ahead with a $219.50 ...

Two complementary studies led by researchers from the Yong Loo Lin School of Medicine, National University of Singapore (NUS ...