After a meeting with the FDA, Scholar Rock is planning a 2026 resubmission of its application seeking approval of apitegromab ...

Like one of her favorite poems describes, columnist Brianna Albers always feels like she's digging herself out of a new hole in her life.

Combining the experimental and approved SMA therapies BIO101 and Spinraza in the lab was found to improve muscle function in ...

Family caregivers express immense devotion to others, but they should also remember self-care, writes columnist.

Spinraza (nusinersen) may help stabilize lung function in people with SMA types 2 and 3, delaying the need for breathing ...

Try these practical tips for travel with SMA, with advice on packing, accessible accommodations, and health management.

Rio Landa, physician whose 14-year-old son, Mateo, is diagnosed with spinal muscular atrophy (SMA) type 2, describes her approach on seeking second opinions or voicing concerns about changes in SMA ...