A major medical milestone took place in May 2025, when doctors at the Children’s Hospital of Philadelphia used CRISPR-based gene editing to treat a child ...
We have written about the promise of gene therapy to correct genetic disease many times. An exciting development happened ...
Gene editing is a group of technologies that enable scientists to precisely alter an organism's DNA. These technologies allow for the addition, removal, or alteration of genetic material at specific ...
Expanding on the Cooperative Center of Excellence in Hematology (CCEH) at Fred Hutchinson Cancer Center’s expertise in providing Human CD34+ HSPCs, we have established a high-efficiency and ...
A new gene-editing technique enables the correction of multiple genetic mutations simultaneously, transforming the prospects ...
In a world first, a bespoke gene-editing therapy benefited one child. Now researchers plan to launch a clinical trial of the ...
In a highly anticipated article, FDA officials Vinay Prasad, M.D., and Martin Makary, M.D., outlined a novel regulatory ...
A quiet hope has started to grow among people living with stubborn cholesterol problems as researchers report early success ...
The FDA approved the genetic therapies for anyone 12 and older suffering from the most severe form of sickle cell disease, a brutal blood disorder that has long been neglected by medical research. The ...
Data presented in a late-breaking presentation at the American Heart Association (AHA) Scientific Sessions 2025- -Phase 1 ...
In a major step forward for cancer care, researchers at ChristianaCare’s Gene Editing Institute have shown that disabling the NRF2 gene with CRISPR technology can reverse chemotherapy resistance in ...