Researchers have found a new way to reactivate fetal hemoglobin without the need for gene-editing therapy, according to a new study.

PHILADELPHIA, PA — Passage Bio, Inc. (Nasdaq: PASG) reported third-quarter financial results and outlined steady progress ...

Alzheimer's disease (AD) is a devastating cause of memory loss and cognitive decline, for which no curative treatment is ...

More than 74,000 participants in clinical trials lost their access to care as a result of Trump administration cuts, ...

To manage the finances of CAR-T therapies, which can cost up to $1 million each, health systems are increasingly using “pay for performance” deals, according to a Nov. 17 article in Specialty Pharmacy ...

The gene therapy will utilize the firm's suprachoroidal vector coAAV-SCS, which it says will be an effective and less burdensome treatment alternative.

PHILADELPHIA, PA — Vittoria Biotherapeutics, Inc. announced it will present interim clinical data from its first-in-human ...

Thermo Fisher executives explain why they picked "Cellicon Valley" for the firm's second U.S. collaboration center and first ...

Alzheimer's disease (AD) is a devastating cause of memory loss and cognitive decline, for which no curative treatment is available.

Researchers said a survey of U.S. adults found 72% say sleepiness sometimes, often or always gets in the way of their ...

A one-time gene therapy using a patient’s own stem cells has effectively cured a deadly immune disorder in 95% of treated children, offering a lasting, donor-free solution to ADA-SCID, known as the ...

A new study led by researchers from the University of Barcelona and the University of Oregon introduces an innovative genetic approach to lowering blood cholesterol. Credit: Shutterstock Researchers ...