A Greer couple is hosting a fundraiser to support a costly gene editing procedure for their two children, who suffer from a ...

Two complementary studies led by researchers from the Yong Loo Lin School of Medicine, National University of Singapore (NUS ...

先天性耳聋患者约2600万，常伴有言语障碍，甚至影响智力发育，一直以来没有临床治疗药物。2022年，复旦大学附属眼耳鼻喉科医院完成全球首例OTOF遗传性耳聋患者基因治疗，成为先天性耳聋首次基因治疗临床实践，成功恢复了患者听力。此后又有7项基因治疗临床 ...

Instead of fixing one of the many genes that can be mutated, the technique addresses a type of mutation they share, a stop ...

医学Medicine2025年10月23日，由复旦大学领衔的全球首个遗传性耳聋基因治疗国际专家共识在Cell Press细胞出版社旗下医学旗舰刊Med上正式发布[1]，并登上Cell Press官网头条。论文题为“International ...

细胞与基因疗法 (Cell and Gene Therapy，CGT)正以前所未有的速度重塑现代医学的边界。自2017年首款 CART 疗法获批以来，CGT ...

Penn and CHOP researchers will utilize the new protocol to distribute customizable drugs that target specific genetic disorders.

YolTech Therapeutics, a clinical-stage biotechnology company developing next-generation in vivo gene editing therapies, today announced that the U.S. Food and Drug Administration (FDA) has cleared the ...

Risk of “acute, serious, and life-threatening” heart inflammation is now on the label of Sarepta's gene therapy for Duchenne ...

Science and Technology Minister Jitendra Singh on Wednesday launched Indias first indigenous CRISPR-based gene therapy for sickle cell disease, which particularly affects the countrys tribal ...

New state-of-the-art facility in Philadelphia provides integrated lab and collaboration space along with tailored guidance to help move advanced therapies from early research to clinical readiness ...