Earlier this year, researchers at Children's Hospital of Philadelphia and Penn created a first-of-its-kind drug customized to ...

Penn and CHOP researchers want to develop urea cycle disorder treatments using CRISPR gene-editing therapy. Get unlimited access to Inquirer.com and The Inquirer App, plus 5 articles each month to ...

In a highly anticipated article, FDA officials Vinay Prasad, M.D., and Martin Makary, M.D., outlined a novel regulatory ...

Alzheimer's disease (AD) is a devastating cause of memory loss and cognitive decline, for which no curative treatment is available.

Alzheimer's disease (AD) is a devastating cause of memory loss and cognitive decline, for which no curative treatment is ...

The FDA’s Marty Makary and Vinay Prasad have laid out a path for CRISPR treatments on demand. An expert weighs in on what it ...

At the Mayo Clinic, cardiologists Peter Noseworthy, M.D., and John Giudicessi, M.D., Ph.D., are uncovering the earliest signs ...

Genetic manipulation – or gene editing – is a concept that describes altering the genetic material (DNA) of an organism.

In this interview, Dr. Kelemen discusses the advantages of lipid-based delivery systems and their potential to expand the reach of CAR T-cell therapies into solid tumor indications.

Artificial intelligence (AI) can predict how well patients with rectal cancer will respond to treatment by analyzing standard ...

A major medical milestone took place in May 2025, when doctors at the Children’s Hospital of Philadelphia used CRISPR-based gene editing to treat a child ...