Scientists at St. Jude Children's Research Hospital and Northwestern University identified a previously unknown treatment ...

Scientists discover a new gene therapy technique that may reverse ALS by restoring vital RNA signals, providing hope for ...

Scientists used a viral gene therapy to restore brain function in mice with SYNGAP1-related disorders, reducing seizures and behavioral symptoms.

As Catalent sets up shop in a new headquarters and refines its corporate image under the ownership of Novo Holdings, the CDMO ...

Researchers said a survey of U.S. adults found 72% say sleepiness sometimes, often or always gets in the way of their ...

N EW ORLEANS – A single injection of a gene-edited protein was deemed productive and safe in patients with dyslipidemia that ...

An experimental gene-editing therapy developed by Crispr Therapeutics is showing promise for treating heart disease.

From revolutionary CRISPR treatment to heavy drinking dangers, here's what you need to know about the latest health research.

Discover how precision biotherapeutics can transform healthcare in India by personalizing treatments based on genetic and ...

Researchers at Tel Aviv University led a large-scale international study that opens a new avenue for treating the fatal ...

A report on gene-editing drugs renews debate around long-term statin use as Indian cardiologists caution that risk assessment ...

Opus Genetics has completed a Type B Regenerative Medicine Advanced Therapy (RMAT) meeting with the US Food and Drug Administration (FDA) regarding OPGx-LCA5, its gene therapy candidate for Leber ...