Researchers have found a new way to reactivate fetal hemoglobin without the need for gene-editing therapy, according to a new study.
Scientists at St. Jude Children's Research Hospital and Northwestern University identified a previously unknown treatment ...
From revolutionary CRISPR treatment to heavy drinking dangers, here's what you need to know about the latest health research.
An experimental gene-editing therapy developed by Crispr Therapeutics is showing promise for treating heart disease.
Scientists discover a new gene therapy technique that may reverse ALS by restoring vital RNA signals, providing hope for ...
A new West Coast biotech has emerged into the busy in vivo cell therapy space, this time with the backing of Nobel Prize-winning CRISPR pioneer Jennifer Doudna, Ph.D. Azalea Therapeutics has bloomed ...
The FDA previously placed two clinical studies on hold, including the Phase III trial in which the liver toxicity occurred. Intellia is working with experts to create a risk management program for nex ...
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Gene Therapy Shows Promise for Cutting LDL in Half in Tough-to-Treat Dyslipidemia
N EW ORLEANS – A single injection of a gene-edited protein was deemed productive and safe in patients with dyslipidemia that ...
Opus Genetics has completed a Type B Regenerative Medicine Advanced Therapy (RMAT) meeting with the US Food and Drug Administration (FDA) regarding OPGx-LCA5, its gene therapy candidate for Leber ...
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