Scientists at St. Jude Children's Research Hospital and Northwestern University identified a previously unknown treatment ...

From revolutionary CRISPR treatment to heavy drinking dangers, here's what you need to know about the latest health research.

Researchers at Tel Aviv University led a large-scale international study that opens a new avenue for treating the fatal ...

Gene therapy is a revolutionary field in modern medicine, offering transformative potential to treat and potentially cure a wide range of genetic and acquired diseases. By addressing the root cause of ...

N EW ORLEANS – A single injection of a gene-edited protein was deemed productive and safe in patients with dyslipidemia that ...

A single one-time gene therapy could free patients with α-thalassemia, a rare and debilitating blood disorder, from the burden of lifelong transfusions. A single one-time gene therapy could free ...

A report on gene-editing drugs renews debate around long-term statin use as Indian cardiologists caution that risk assessment ...

The agency is establishing a network of care centers to expand access to regenerative medicine beyond regions served by major ...

Opus Genetics has completed a Type B Regenerative Medicine Advanced Therapy (RMAT) meeting with the US Food and Drug Administration (FDA) regarding OPGx-LCA5, its gene therapy candidate for Leber ...