The U.S. Food and Drug Administration is tightening restrictions on a gene therapy used to treat Duchenne muscular dystrophy ...

Coave Therapeutics has announced its lead gene therapy program, CoTx-10, for the treatment of retinal vascular diseases, such ...

Taysha Gene Therapies Inc. (NASDAQ: TSHA) is a must-buy penny stock to buy now. On November 13, Piper Sandler analyst Biren ...

Fred Hutch bioengineer Dr. Matthias Stephan is working to develop a special foam that could help make gene therapy for blood ...

The US FDA has tightened the use of a Duchenne muscular dystrophy gene therapy after two teenage patients died from acute ...

Through substantial leadership turnover and workforce cuts, the FDA has continued to support the advanced therapy sector, ...

Krystal Biotech drives Vyjuvek growth, premium margins, global expansion, a $1B goal, and pipeline data ahead with a $219.50 ...

Earlier this year, researchers at Children's Hospital of Philadelphia and Penn created a first-of-its-kind drug customized to ...

By adding a microRNA molecule to ALS models, Tel Aviv University, Ben-Gurion University and Weizmann Institute researchers ...

Sarepta must also run a post-marketing study for Elevidys to better assess the risk of serious liver injury in patients dosed ...

The Food and Drug Administration is adding a new warning to a gene therapy linked to two patient deaths earlier this year.