FDA tightens Duchenne gene therapy after deaths of two teens

The U.S. Food and Drug Administration is tightening restrictions on a gene therapy used to treat Duchenne muscular dystrophy ...
Ophthalmology Times

Coave Therapeutics reveals lead gene therapy program, CoTx-10

Coave Therapeutics has announced its lead gene therapy program, CoTx-10, for the treatment of retinal vascular diseases, such ...
BioSpaceOpinion

Opinion: How the FDA Is Accelerating Cell and Gene Therapy’s Next Chapter

Through substantial leadership turnover and workforce cuts, the FDA has continued to support the advanced therapy sector, ...

Researchers to test gene therapy for rare diseases with a new FDA trial protocol

Earlier this year, researchers at Children's Hospital of Philadelphia and Penn created a first-of-its-kind drug customized to ...
ExtremeTech

What is gene therapy?

In medicine these days, the word "gene" shows up in all sorts of different contexts and conjugations. There's genetics, of course, and there's genomics. Then there's meta-genomics -- and don't forget ...

US FDA Restricts Duchenne Gene Therapy Following Fatal Liver Failure Cases in Teens

The US FDA has tightened the use of a Duchenne muscular dystrophy gene therapy after two teenage patients died from acute ...
Fred Hutchinson Cancer Center

Scientists see foam as starting point of a path to bedside gene therapy

Fred Hutch bioengineer Dr. Matthias Stephan is working to develop a special foam that could help make gene therapy for blood ...
Los Angeles Magazine

What Is Gene Therapy?

This sponsored article was provided by a partner and is not editorial content from Los Angeles Magazine or the Engine Vision Media Network. Every cell in your body holds a unique genetic code within ...
The Times of Israel on MSN

In world first, Israeli scientists use RNA-based gene therapy to stop ALS deterioration

By adding a microRNA molecule to ALS models, Tel Aviv University, Ben-Gurion University and Weizmann Institute researchers ...